New Atlas22h
RNA therapy an effective alternative to lifelong, painful eye injections
An RNA-editing gene therapy has been developed that switches off the key driver of common eye conditions affecting diabetics ...
BioSpace4d
Patient Death Taints Otherwise Positive Data for Beam’s Sickle Cell Gene Therapy
BEAM-101 seems to be competitive with approved sickle cell treatments, William Blair analysts said in a note to investors, ...
GEN3d
Navigating Quality Control and Release Testing in Cell and Gene Therapy Development
In this GEN webinar, our speakers will present important considerations for quality control testing for biosafety and product ...
Stem cells can tailor their role in gene therapy based on the underlying disease, study suggests
RCCS San Raffaele Scientific Institute in Milan researchers have discovered that hematopoietic stem cells (HSCs) adapt their lineage commitment during gene therapy based on the underlying genetic ...
Becker's Hospital Review3d
Sickle cell patient dies in gene-therapy trial
Beam Therapeutics' early clinical data shows promising results for sickle cell disease treatment using CRISPR gene editing tool. One patient died ...
How this ‘Switchable’ CAR-T Therapy Sets its Sights on Deadly Brain Cancer
SYNC, its first homegrown CAR-T therapy, one of the first to show promise in treating certain types of brain cancers. This ...
University of Pennsylvania gene therapy spinout Interius BioTherapeutics doses patient, achieves CAR therapy first
Its lead gene therapy candidate has the potential to be faster, less expensive, and more widely available than current CAR T ...
Gene Therapy Developer Beam Therapeutics Reports One Patient Death In Early-Stage Sickle Cell Disease Trial
Beam Therapeutics enrolls 35 patients in BEACON trial for BEAM-101 in sickle cell disease, with promising early safety and ...
Baylor College of Medicine4d
Grants awarded to leading investigators at Baylor's Center for Cell and Gene Therapy
Three investigators at Baylor College of Medicine’s (BCM) Center for Cell and Gene Therapy Institute (CAGT) have been awarded G-Rex Grants totaling $475,000 by ScaleReady, in collaboration with Wilson ...
Sickle cell patient dies in Beam study of base editing therapy
The death, which investigators linked to a preparatory chemo treatment rather than Beam's medicine, highlights the risks of ...
WuXi AppTec Says Advanced Therapy Unit Hit Despite Revenue Beat
WuXi AppTec Co. posted better-than-expected third-quarter revenue despite concerns over a US bill seeking to block the ...
Managed Healthcare Executive9d
Managed Care Experts Agree on Gene Therapy’s Clinical Benefits for Inherited Blood Disorders But See Hurdles for Coverage
In-depth interviews and an online survey found support for gene therapy as a treatment for inherited blood disorders, but ...