High dose TSHA-102 was generally well tolerated with no SAEs or DLTs in two adolescent/adult patients and one <a target=_blank href= ...

High Investment and Government Initiatives to Boost Rare Diseases Treatment ModalitiesRockville, MD, Nov. 13, 2024 (GLOBE NEWSWIRE) -- According to Fact.MR, a market research and competitive ...

Findings suggest that PER3 gene variants prevent adrenal adaptation to winter daylight ... often linked to increases in ...

Let's go over the whole cast of Sonic The Hedgehog characters and discuss which are the best in the franchise.

the company delivered an oral presentation highlighting preclinical data for PBFT02 at the European Society of Gene & Cell Therapy (ESGCT) conference. The presentation reviewed the robust preclinical ...

GenSight Biologics (Euronext: SIGHT, ISIN: FR0013183985, PEA-PME eligible), a biopharma company focused on developing and commercializing innovative gene therapies for retinal neurodegenerative ...